Authors Isabelle Sermet-Gaudelus, John P. Clancy, David P. Nichols, Jerry A. Nick, Kris De Boeck, George M. Solomon, Marcus A. Mall,h,i, James Bolognese, Florilene Bouisset, Wilhelmina den Hollander, Nicolas Paquette-Lamontagne, Nigel Tomkinson, Noreen Henig, J. Stuart Elborn and Steven M. Rowe
References J Cyst Fibros. 2018 Nov 19. pii: S1569-1993(18)30914-7. doi: 10.1016/j.jcf.2018.10.015
Keywords Antisense oligonucleotide, Clinical trial, Cystic Fibrosis Transmembrane Conductance Regulator delta F508, Nasal potential difference, Pulmonary Medicine