Therapeutic benefit observed with the CFTR potentiator, ivacaftor, in a CF patient homozygous for the W1282X CFTR nonsense mutation
Creation and characterization of an airway epithelial cell line for stable expression of CFTR variants
CFTR potentiator therapy ameliorates impaired insulin secretion in CF patients with a gating mutation
Alterations in blood leukocytes of G551D-bearing cystic fibrosis patients undergoing treatment with ivacaftor.
