The ECFS-CTN cannot guarantee that the information provided here is comprehensive. Please go to the link for detailed and up-to-date information on study background, eligibility criteria, study design, outcome measures, study status, participating sites, sponsor contact information and timelines.

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Study Name on (link is external)
Study of Ivacaftor in Cystic Fibrosis Subjects 2 Through 5 Years of Age With a CTFR Gating Mutation
Study DrugIvacaftor (VX770)
Type of Study DrugCFTR Modulation
Study TitleA Phase 3, 2-Part, Open-Label Study to Evaluate the Safety, Pharmacokinetics and Pharmacodynamics of Ivacaftor in Subjects With Cystic Fibrosis Who Are 2 Through 5 Years of Age and Have a CFTR Gating Mutation
Study Phase3
Study SponsorVertex

Link on (link is external) (link is external)

Participating ECFS-CTN sitesUK: London
Age2-5 Years