Long-term health effects of real-world use of ivacaftor by people with cystic fibrosis who have non-G551D-CFTR gating mutations
CFTR modulators: A case where Triple therapy induced rash resolved on its own, without stopping the drug
Treatment of Idiopathic Chronic Pancreatitis (ICP) with ivacaftor in a Cystic Fibrosis (CF) carrier who also had a second inherited risk factor for pancreatitis called Methylmalonic Acidemia
Description of children who changed diagnosis from indeterminate newborn screening to cystic fibrosis
Outcomes and endpoints reported in studies of pulmonary exacerbations in people with cystic fibrosis (CF): a systematic review
Prevalence, management and outcome of Italian infants with cystic fibrosis screening positive inconclusive diagnosis