Can we measure effectiveness of new cystic fibrosis treatments in improving lung health in children with cystic fibrosis aged less than 2 years of age during clinical trials conducted for the approval of new medicines?
How important are different trials features when people decide whether to take part in cystic fibrosis clinical trials?
Changes in symptom scores as a potential clinical endpoint for studies of cystic fibrosis pulmonary exacerbation treatment
Factors influencing clinical trial participation for adult and pediatric patients with cystic fibrosis
A four week trial of hypertonic saline in children with mild cystic fibrosis lung disease: Effect on mucociliary clearance and clinical outcomes