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Home > Can we measure effectiveness of new cystic fibrosis treatments in improving lung health in children with cystic fibrosis aged less than 2 years of age during clinical trials conducted for the approval of new medicines?

Can we measure effectiveness of new cystic fibrosis treatments in improving lung health in children with cystic fibrosis aged less than 2 years of age during clinical trials conducted for the approval of new medicines?

Resource Type

CF Research News

Authors

Tim Lee, Kate Hill, Daan Caudri, Pierluigi Ciet, Gwyneth Davies, Jane C Davies, Anna-Maria Dittrich, Anders Lindblad, Paul McNally, Philippe Reix, Clare Saunders, Isabelle Sermet-Gaudelus, Mirjam Stahl, Harm A.W.M. Tiddens, Hettie M. Janssens

References

J Cyst Fibros. 2025 Jul 3:S1569-1993(25)01517-6.  doi: 10.1016/j.jcf.2025.06.003

Document

File JCF-D-25-00055R1_FINAL_Janssens_270725.docx [1]

Keywords

Chest CT [2]
Chest MRI [3]
clinical trials [4]
infants [5]
Infection [6]
Inflammation [7]
Multiple breath washout [8]
Paediatrics [9]
Pulmonary endpoints [10]

Date

Saturday, July 5, 2025

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [11]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu:443/resource-article/cf-research-news/can-we-measure-effectiveness-new-cystic-fibrosis-treatments

Links
[1] https://www.ecfs.eu:443/sites/default/files/cf-research-article-files/JCF-D-25-00055R1_FINAL_Janssens_270725.docx [2] https://www.ecfs.eu:443/research-article-keywords/chest-ct [3] https://www.ecfs.eu:443/research-article-keywords/chest-mri [4] https://www.ecfs.eu:443/research-article-keywords/clinical-trials [5] https://www.ecfs.eu:443/research-article-keywords/infants [6] https://www.ecfs.eu:443/research-article-keywords/infection [7] https://www.ecfs.eu:443/research-article-keywords/inflammation [8] https://www.ecfs.eu:443/research-article-keywords/multiple-breath-washout [9] https://www.ecfs.eu:443/research-article-keywords/paediatrics [10] https://www.ecfs.eu:443/research-article-keywords/pulmonary-endpoints [11] https://www.ecfs.eu:443/resource-guideline-type/other-guidelines