European Cystic Fibrosis Society (ECFS)
Published on European Cystic Fibrosis Society (ECFS) (https://www.ecfs.eu)

Home > Effectiveness of ivacaftor in cystic fibrosis patients with non-G551D gating mutations.

Effectiveness of ivacaftor in cystic fibrosis patients with non-G551D gating mutations.

Resource Type

CF Research News

Authors

Guimbellot J, Solomon GM, Baines A, Heltshe SL, VanDalfsen J, Joseloff E, Sagel SD, Rowe SM; GOALe(2) Investigators.

References

J Cyst Fibros. 2018 Apr 20. pii: S1569-1993(18)30090-0. doi: 10.1016/j.jcf.2018.04.004.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

CFTR potentiator [3]
clinical trials [4]
Gating mutation [5]
Ivacaftor [6]

Date

Friday, April 20, 2018

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [7]
Terms & Conditions Privacy policy  Accessibility Sitemap Contact 
© EUROPEAN CYSTIC FIBROSIS SOCIETY 2025. All rights reserved. Website by VidaVia (link is external)
European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/effectiveness-ivacaftor-cystic-fibrosis-patients-non-g551d-gating

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-18-00070R1_FINAL_Rowe_220418.pdf [2] https://www.ncbi.nlm.nih.gov/pubmed/?term=Effectiveness%20of%20ivacaftor%20in%20cystic%20fibrosis%20Patients%20with%20non-G551D%20gating%20mutations [3] https://www.ecfs.eu/research-article-keywords/cftr-potentiator [4] https://www.ecfs.eu/research-article-keywords/clinical-trials [5] https://www.ecfs.eu/research-article-keywords/gating-mutation [6] https://www.ecfs.eu/research-article-keywords/ivacaftor [7] https://www.ecfs.eu/resource-guideline-type/other-guidelines