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Home > Different Drugs, Different Results: What New CF Treatments Can Offer

Different Drugs, Different Results: What New CF Treatments Can Offer

Resource Type

CF Research News

Authors

Noelia Rodriguez Mier, Isabelle Callebaut, Marijke Proesmans, Eva Van Braeckel, Stephanie Van Biervliet, Mieke Boon, Anabela Santo Ramalho, François Vermeulen

References

2026 Mar;25(2):314-318. doi: 10.1016/j.jcf.2025.12.018. Epub 2025 Dec 31.

Document

File JCF-D-25-00321R1_FINAL_Rodriguez Mier_26012026.docx [1]

Keywords

CFTR modulators [2]
Cystic fibrosis [3]
Elexacaftor [4]
In vitro functional assays [5]
Patientderived intestinal organoids [6]
Personalized therapy [7]
Rare CFTR variants [8]
Theratyping [9]
Vanzacaftor [10]

Date

Sunday, March 22, 2026

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [11]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/different-drugs-different-results-what-new-cf-treatments-can-offer

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-25-00321R1_FINAL_Rodriguez%20Mier_26012026.docx [2] https://www.ecfs.eu/research-article-keywords/cftr-modulators [3] https://www.ecfs.eu/research-article-keywords/cystic-fibrosis [4] https://www.ecfs.eu/research-article-keywords/elexacaftor [5] https://www.ecfs.eu/research-article-keywords/vitro-functional-assays [6] https://www.ecfs.eu/research-article-keywords/patientderived-intestinal-organoids [7] https://www.ecfs.eu/research-article-keywords/personalized-therapy [8] https://www.ecfs.eu/research-article-keywords/rare-cftr-variants [9] https://www.ecfs.eu/research-article-keywords/theratyping [10] https://www.ecfs.eu/research-article-keywords/vanzacaftor [11] https://www.ecfs.eu/resource-guideline-type/other-guidelines