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Home > Early access to the CFTR modulator treatment helps severely ill infant with Cystic Fibrosis

Early access to the CFTR modulator treatment helps severely ill infant with Cystic Fibrosis

Resource Type

CF Research News

Authors

Paul D Robinson, Claire E Wainwright, Elizabeth Shevill

References

J Cyst Fibros. 2025 Aug 18:S1569-1993(25)01565-6.  doi: 10.1016/j.jcf.2025.08.006

Document

File JCF-D-25-00202R1_FINAL_Shevill_25082025.docx [1]

Keywords

Ethical review [2]
Multidisciplinary team shared goals [3]
Reduced hospital admissions [4]
Urgent paediatric care [5]

Date

Monday, August 4, 2025

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [6]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/early-access-cftr-modulator-treatment-helps-severely-ill-infant

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-25-00202R1_FINAL_Shevill_25082025.docx [2] https://www.ecfs.eu/research-article-keywords/ethical-review [3] https://www.ecfs.eu/research-article-keywords/multidisciplinary-team-shared-goals [4] https://www.ecfs.eu/research-article-keywords/reduced-hospital-admissions [5] https://www.ecfs.eu/research-article-keywords/urgent-paediatric-care [6] https://www.ecfs.eu/resource-guideline-type/other-guidelines