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Home > Long-term health effects of real-world use of ivacaftor by people with cystic fibrosis who have non-G551D-CFTR gating mutations

Long-term health effects of real-world use of ivacaftor by people with cystic fibrosis who have non-G551D-CFTR gating mutations

Resource Type

CF Research News

Authors

Nicholas J. Simmonds, C. Kors van der Ent, Carla Colombo, Nils Kinnman, Cynthia DeSouza, Teja Thorat, Marci L. Chew, Keval Chandarana, Carlo Castellani

References

J Cyst Fibros. 2022 May 22;S1569-1993(22)00141-2. doi: 10.1016/j.jcf.2022.05.007.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Theme

Care of patients with CF [3]
Pulmonology [4]

Keywords

CFTR gating mutation [5]
Healthcare resource utilization [6]
Ivacaftor [7]
Lung function [8]
Real-world experience [9]

Date

Sunday, May 22, 2022

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [10]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/long-term-health-effects-real-world-use-ivacaftor-people-cystic

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-22-00063R2_FINAL_Simmonds_10072022.pdf [2] https://pubmed.ncbi.nlm.nih.gov/35613999/ [3] https://www.ecfs.eu/research-article-themes/care-patients-cf [4] https://www.ecfs.eu/research-article-themes/pulmonology [5] https://www.ecfs.eu/research-article-keywords/cftr-gating-mutation [6] https://www.ecfs.eu/research-article-keywords/healthcare-resource-utilization [7] https://www.ecfs.eu/research-article-keywords/ivacaftor [8] https://www.ecfs.eu/research-article-keywords/lung-function [9] https://www.ecfs.eu/research-article-keywords/real-world-experience [10] https://www.ecfs.eu/resource-guideline-type/other-guidelines