Antisense oligonucleotide as a novel therapy for people with CF affected by the W1282X mutation
Resource Type
CF Research News
Authors
References
J Cyst Fibros. 2021 Dec 28;S1569-1993(21)02172-X. doi: 10.1016/j.jcf.2021.12.012.
Document
Link
Theme
Keywords
drug development [5]
Exon skipping [6]
Date
Tuesday, December 28, 2021
Featured resource article
Yes
Resource - Guideline Type
Other Guidelines [7]