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Home > Comparison of gene editing methods to correct the W1282X mutation

Comparison of gene editing methods to correct the W1282X mutation

Resource Type

CF Research News

Authors

Lúcia Santos, Karen Mention, Kader Cavusoglu-Doran, David J Sanz, Mafalda Bacalhau, Miquéias Lopes-Pacheco, Patrick T Harrison, Carlos M Farinha

References

J Cyst Fibros. 2021 Jun 5;S1569-1993(21)00167-3. doi: 10.1016/j.jcf.2021.05.014.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

CFTR [3]
CRISPR/Cas12a [4]
CRISPR/Cas9 [5]
human bronchial epithelial cells [6]
W1282X [7]

Date

Saturday, June 5, 2021

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [8]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/comparison-gene-editing-methods-correct-w1282x-mutation

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-21-00067R2_FINAL_Farinha_100721.pdf [2] https://pubmed.ncbi.nlm.nih.gov/34103250/ [3] https://www.ecfs.eu/research-article-keywords/cftr [4] https://www.ecfs.eu/research-article-keywords/crisprcas12a [5] https://www.ecfs.eu/research-article-keywords/crisprcas9 [6] https://www.ecfs.eu/research-article-keywords/human-bronchial-epithelial-cells [7] https://www.ecfs.eu/research-article-keywords/w1282x [8] https://www.ecfs.eu/resource-guideline-type/other-guidelines