Targeting G542X CFTR Nonsense Alleles With ELX-02 Restores CFTR Function in Human-Derived Intestinal Organoids
Resource Type
CF Research News
Authors
References
J Cyst Fibros. 2021 Feb 5;S1569-1993(21)00028-X. doi: 10.1016/j.jcf.2021.01.009.
Document
Link
Keywords
ELX-02 [3]
NB124 [4]
Nonsense allele [5]
Organoid [6]
Read-through [7]
Date
Friday, February 5, 2021
Featured resource article
Yes
Resource - Guideline Type
Other Guidelines [8]