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Lumacaftor/ivacaftor in people with cystic fibrosis with an A455E-CFTR mutation

Resource Type

CF Research News

Authors

Gitte Berkers, Renske van der Meer, Harry Heijerman, Jeffrey M Beekman, Sylvia F Boj, Robert G J Vries, Peter van Mourik, Jamie R Doyle, Paul Audhya, Zheng Jason Yuan, Nils Kinnman, C Kors van der Ent

References

J Cyst Fibros. 2020 Nov 25;S1569-1993(20)30910-3. doi: 10.1016/j.jcf.2020.11.007.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

A455E–CFTR [3]
Crossover study [4]
Cystic fibrosis [5]
Lumacaftor/ivacaftor [6]

Date

Wednesday, November 25, 2020

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [7]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/lumacaftorivacaftor-people-cystic-fibrosis-a455e-cftr-mutation

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-20-00388R2_FINAL_VanDerEnt_210221.pdf [2] https://pubmed.ncbi.nlm.nih.gov/33249003/ [3] https://www.ecfs.eu/research-article-keywords/a455e%E2%80%93cftr [4] https://www.ecfs.eu/research-article-keywords/crossover-study [5] https://www.ecfs.eu/research-article-keywords/cystic-fibrosis [6] https://www.ecfs.eu/research-article-keywords/lumacaftorivacaftor [7] https://www.ecfs.eu/resource-guideline-type/other-guidelines