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Home > Ivacaftor in Cystic Fibrosis With Residual Function: Lung Function Results From an N-of-1 Study

Ivacaftor in Cystic Fibrosis With Residual Function: Lung Function Results From an N-of-1 Study

Resource Type

CF Research News

Authors

Jerry A. Nick, Connie St. Clair, Marion C. Jones, Lan Lan, Mark Higgins

References

J Cyst Fibros. 2019 Nov 26. pii: S1569-1993(19)30897-5. doi: 10.1016/j.jcf.2019.09.013.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

Bayesian hierarchical model [3]
Cystic fibrosis transmembrane conductance regulator [4]
forced expiratory volume [5]
Ivacaftor [6]
Residual CFTR function [7]

Date

Tuesday, November 26, 2019

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [8]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/ivacaftor-cystic-fibrosis-residual-function-lung-function-results

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-19-00255R3_FINAL_Nick_090120.pdf [2] https://pubmed.ncbi.nlm.nih.gov/31784217-ivacaftor-in-cystic-fibrosis-with-residual-function-lung-function-results-from-an-n-of-1-study/?from_single_result=Ivacaftor%20in%20Cystic%20Fibrosis%20With%20Residual%20Function%3A%20Lung%20Function%20Results%20From%20an%20N-of-1%20Study [3] https://www.ecfs.eu/research-article-keywords/bayesian-hierarchical-model [4] https://www.ecfs.eu/research-article-keywords/cystic-fibrosis-transmembrane-conductance-regulator [5] https://www.ecfs.eu/research-article-keywords/forced-expiratory-volume [6] https://www.ecfs.eu/research-article-keywords/ivacaftor [7] https://www.ecfs.eu/research-article-keywords/residual-cftr-function [8] https://www.ecfs.eu/resource-guideline-type/other-guidelines