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Home > Speeding up access to new drugs for Cystic Fibrosis: Considerations for clinical trial design and delivery

Speeding up access to new drugs for Cystic Fibrosis: Considerations for clinical trial design and delivery

Resource Type

CF Research News

Authors

On behalf of the European CF Society (ECFS) Strategic Planning Task Force on ‘Speeding up access to new drugs for CF’: Margarida Amaral, Kris de Boeck, Jane C Davies, Pavel Drevinek, J Stuart Elborn, Eitan Kerem, Tim Lee

References

J Cyst Fibros. [1] 2019 Jul 11. pii: S1569-1993(19)30815-X. doi: 10.1016/j.jcf.2019.06.011.

Document

PDF icon CF Research News Article [2]

Link

Scientific Abstract [3]

Keywords

CFTR modulators [4]
Clinical trial design [5]

Date

Thursday, July 11, 2019

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [6]
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Source URL:https://www.ecfs.eu/resource-article/cf-research-news/speeding-access-new-drugs-cystic-fibrosis-considerations-clinical

Links
[1] https://www.ncbi.nlm.nih.gov/pubmed/?term=Speeding+up+access+to+new+drugs+for+Cystic+Fibrosis%3A+Considerations+for+clinical+trial+design+and+delivery# [2] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-19-00092R3_FINAL_Davies_170819.pdf [3] https://www.ncbi.nlm.nih.gov/pubmed/?term=Speeding%20up%20access%20to%20new%20drugs%20for%20Cystic%20Fibrosis%3A%20Considerations%20for%20clinical%20trial%20design%20and%20delivery [4] https://www.ecfs.eu/research-article-keywords/cftr-modulators [5] https://www.ecfs.eu/research-article-keywords/clinical-trial-design [6] https://www.ecfs.eu/resource-guideline-type/other-guidelines