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Home > Theranostics by testing CFTR modulators in patient-derived materials: the current status and a proposal for subjects with rare CFTR mutations

Theranostics by testing CFTR modulators in patient-derived materials: the current status and a proposal for subjects with rare CFTR mutations

Resource Type

CF Research News

Authors

Amaral MD, de Boeck K; ECFS Strategic Planning Task Force on ‘Speeding up access to new drugs for CF

References

J Cyst Fibros. 2019 Jul 17. pii: S1569-1993(19)30814-8. doi: 10.1016/j.jcf.2019.06.010. 

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Date

Wednesday, July 17, 2019

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [3]
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Source URL:https://www.ecfs.eu/resource-article/cf-research-news/theranostics-testing-cftr-modulators-patient-derived-materials

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-19-00101R2_FINAL_Davies_Review_170819.pdf [2] https://www.ncbi.nlm.nih.gov/pubmed/?term=Theranostics%20by%20testing%20CFTR%20modulators%20in%20patient-derived%20materials%3A%20the%20current%20status%20and%20a%20proposal%20for%20subjects%20with%20rare%20CFTR%20mutations [3] https://www.ecfs.eu/resource-guideline-type/other-guidelines