European Cystic Fibrosis Society (ECFS)
Published on European Cystic Fibrosis Society (ECFS) (https://www.ecfs.eu)

Home > GLPG1837, a CFTR potentiator, in p.Gly551Asp (G551D)-CF patients: An open-label, single-arm, phase 2a study (SAPHIRA1)

GLPG1837, a CFTR potentiator, in p.Gly551Asp (G551D)-CF patients: An open-label, single-arm, phase 2a study (SAPHIRA1)

Resource Type

CF Research News

Authors

Davies JC, Van de Steen O, van Koningsbruggen-Rietschel S, Drevinek P, Derichs N, McKone EF, Kanters D, Allamassey L, Namour F, de Kock H, Conrath K

References

J Cyst Fibros. 2019 May 27. pii: S1569-1993(19)30111-0. doi: 10.1016/j.jcf.2019.05.006. 

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Date

Monday, May 27, 2019

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [3]
Terms & Conditions Privacy policy  Accessibility Sitemap Contact 
© EUROPEAN CYSTIC FIBROSIS SOCIETY 2025. All rights reserved. Website by VidaVia (link is external)
European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/glpg1837-cftr-potentiator-pgly551asp-g551d-cf-patients-open-label

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-19-00070R2_FINAL_Conrath_270719.pdf [2] https://www.ncbi.nlm.nih.gov/pubmed/?term=GLPG1837%2C%20A%20CFTR%20POTENTIATOR%2C%20IN%20p.Gly551Asp%20%28G551D%29-CF%20PATIENTS%3A%20AN%20OPEN-LABEL%2C%20SINGLE-ARM%2C%20PHASE%202a%20STUDY%20%28SAPHIRA1%29 [3] https://www.ecfs.eu/resource-guideline-type/other-guidelines