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Home > Antisense oligonucleotide eluforsen is safe and improves respiratory symptoms in F508DEL cystic fibrosis.

Antisense oligonucleotide eluforsen is safe and improves respiratory symptoms in F508DEL cystic fibrosis.

Resource Type

CF Research News

Authors

Drevinek P, Pressler T, Cipolli M, De Boeck K, Schwarz C, Bouisset F, Boff M, Henig N, Paquette-Lamontagne N, Montgomery S, Perquin J, Tomkinson N, den Hollander W, Elborn JS

References

J Cyst Fibros. 2019 Jun 7. pii: S1569-1993(19)30766-0. doi: 10.1016/j.jcf.2019.05.014

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

Antisense oligonucleotide [3]
CFQ-R RSS [4]
Clinical trial [5]
Delta F508 [6]
Pulmonary Medicine [7]

Date

Friday, June 7, 2019

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [8]
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Source URL:https://www.ecfs.eu/resource-article/cf-research-news/antisense-oligonucleotide-eluforsen-safe-and-improves-respiratory

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-19-00124R1_FINAL_Elborn_110719.pdf [2] https://www.ncbi.nlm.nih.gov/pubmed/?term=ANTISENSE%20OLIGONUCLEOTIDE%20ELUFORSEN%20IS%20SAFE%20AND%20IMPROVES%20RESPIRATORY%20SYMPTOMS%20IN%20F508DEL%20CYSTIC%20FIBROSIS [3] https://www.ecfs.eu/research-article-keywords/antisense-oligonucleotide [4] https://www.ecfs.eu/research-article-keywords/cfq-r-rss [5] https://www.ecfs.eu/research-article-keywords/clinical-trial [6] https://www.ecfs.eu/research-article-keywords/delta-f508 [7] https://www.ecfs.eu/research-article-keywords/pulmonary-medicine [8] https://www.ecfs.eu/resource-guideline-type/other-guidelines