European Cystic Fibrosis Society (ECFS)
Published on European Cystic Fibrosis Society (ECFS) (https://www.ecfs.eu)

Home > Mini-guts help test responses to CFTR modulators in people with cystic fibrosis carrying F508del

Mini-guts help test responses to CFTR modulators in people with cystic fibrosis carrying F508del

Resource Type

CF Research News

Authors

Noelia Rodriguez Mier, Senne Cuyx, Kris De Boeck, Marijke Proesmans, Mieke Boon, Lieven Dupont, Kaline Arnauts, Elke De Wachter, Stephanie Van Biervliet, Monique Lequesne, Vicky Nowé, Hedwige Boboli, Anabela Santo Ramalho, François Vermeulen, on behalf of

References

J Cyst Fibros. 2025 Aug 29:S1569-1993(25)01570-X.  doi: 10.1016/j.jcf.2025.08.011

Document

File JCF-D-25-00168R2_FINAL_Rodriguez Mier_01092025.docx [1]

Keywords

CFTR functional assays [2]
Cystic fibrosis [3]
F508del [4]
Patient derived intestinal organoids [5]

Date

Monday, August 4, 2025

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [6]
Terms & Conditions Privacy policy  Accessibility Sitemap Contact 
© EUROPEAN CYSTIC FIBROSIS SOCIETY 2025. All rights reserved. Website by VidaVia (link is external)
European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/mini-guts-help-test-responses-cftr-modulators-people-cystic

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-25-00168R2_FINAL_Rodriguez%20Mier_01092025.docx [2] https://www.ecfs.eu/research-article-keywords/cftr-functional-assays [3] https://www.ecfs.eu/research-article-keywords/cystic-fibrosis [4] https://www.ecfs.eu/research-article-keywords/f508del [5] https://www.ecfs.eu/research-article-keywords/patient-derived-intestinal-organoids [6] https://www.ecfs.eu/resource-guideline-type/other-guidelines