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Home > Evaluating the Effectiveness of a Novel CF Medication for People Without Common Cystic Fibrosis-causing Genetic Mutations

Evaluating the Effectiveness of a Novel CF Medication for People Without Common Cystic Fibrosis-causing Genetic Mutations

Resource Type

CF Research News

Authors

Daniel Lupas, Frank Y Chou, Mohammad Abdullah Al Hakani, Ishita Kuthiala, Arjuna Srikrishnaraj, Xuan Li, Naomi Potter, Bradley S Quon

References

J Cyst Fibros. 2024 Sep;23(5):950-958. doi: 10.1016/j.jcf.2024.07.012. Epub 2024 Jul 23.

Document

PDF icon CF Research News Article [1]

Link

Scientific Abstract [2]

Keywords

CFTR modulator [3]
Elexacaftor/tezacaftor/ivacaftor [4]
Non-F508del mutation [5]

Date

Monday, September 23, 2024

Featured resource article

Yes

Resource - Guideline Type

Other Guidelines [6]
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European Cystic Fibrosis Society (ECFS)

Source URL:https://www.ecfs.eu/resource-article/cf-research-news/evaluating-effectiveness-novel-cf-medication-people-without-common

Links
[1] https://www.ecfs.eu/sites/default/files/cf-research-article-files/JCF-D-24-00154R2_FINAL_Quon_070924.pdf [2] https://pubmed.ncbi.nlm.nih.gov/39048464/ [3] https://www.ecfs.eu/research-article-keywords/cftr-modulator [4] https://www.ecfs.eu/research-article-keywords/elexacaftortezacaftorivacaftor [5] https://www.ecfs.eu/research-article-keywords/non-f508del-mutation [6] https://www.ecfs.eu/resource-guideline-type/other-guidelines